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When the Food and Drug Administration recently approved the first gene therapy to treat metachromatic leukodystrophy, a fatal childhood inherited brain disease, Maria Kefalas was…
Calliope Joy Carr, a Bala Cynwyd girl who had a rare degenerative genetic disease and inspired many to make life better for children like her…
Maria Kefalas, a renowned St. Joseph’s University sociologist, has published a new book about the grief of raising a daughter destined to die, writes…
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